Vertex Pharmaceuticals is developing a CF drug called VX-770, which is designed to treat the underlying cause of cystic fibrosis — a faulty gene and its protein product called CFTR. Only 4% of the CF population has the G551D mutation which this drug if FDA approved hopefully going to be available around the end of 2012.
This is huge!! Not only is my son part of this 4% but this will help with opening up the future for other possible discovery's. I can not express how happy this has made me and my family. The joy I feel is indescribable. As such life is good!
Live Life Now.1.2.3....
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